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Rare diseases - understanding the particularities of designing and conducting a therapeutic trial

Training in the specificities of therapeutic trials for rare diseases.

  • Type of training
    Diploma course
  • Diplôme
    DESIU
  • Target audience
    Doctor
    Paramedical
    Pharmacist
    Other audiences
  • Discipline
    Neurology
    Therapeutics
  • Duration
    1 year
  • Teachers in charge
    Prof. Olivier BLIN
  • School
    Medicine

  • Présentation de la formation

    Pedagogical objectives

    Learn how to build and run a therapeutic trial for rare diseases:

    • understand the environment of rare diseases and therapeutic trialsknow how to
    • analyze and criticize a protocolknow

    the

    • useful methodologies and tools (types of trial, statistical tools, etc.

    ) for building a trialunderstand the steps leading to basic research in clinical research.

    • understand

      • the

    • stages leading from basic research to clinical researchknow

      • the

    • regulatory bases for therapeutic trials in rare diseases (authorization, registration,

      • monitoring) and the specificities of pediatric trials,

    • be
    • aware of
    • the
    • ethical and societal dimensions of NCM research (pediatric trials, drug costs, etc.

      • ).

    • )


    Inform and train professionals in the specificities of therapeutic trials on rare diseases, with the aim of being able to participate in, design and run a therapeutic trial in the field of rare diseases

    .

    Partners

    • University of DijonUniversity of
    • LilleUniversity

      • of

    • Lyon 1

    PRESENTATION - DESIU Rare Diseases - Understanding the particularities of designing and conducting a therapeutic trial

  • Autorisation pédagogique

    Eligibility

    • Doctors, pharmacists, medical or pharmacy internsNurses
    • , paramedicsScientists
    • , research professionals, pharmaceutical companiesRepresentatives

      • of regulatory

    • authoritiesRepresentatives
    • of associationsOther
    • professions: on file

      • .

    Admission procedure

    • Applications for pre-registration
    • 2022-2023Application
    • validation
    • by e-mail, following a meeting of the pedagogical committeeRegistration
    • : following pre-registration validation by the pedagogical committee

      • .

    • Online registration on the partner universities' websites (based on letter of approval from the pedagogical committee).

    Educational information and admission authorizations

    Teacher in charge
    Pr Olivier BLIN
    Email : olivier.blin@ap-hm.fr

  • Inscription administrative

    Administrative registration information:

    Email: umfcs-desu@univ-amu.fr
    Fatma FATHI
    Tél : 04 91 32 45 91
    Marine HANAOUI
    Tél : 04 91 32 46 48
    Annie DESCHAMPS
    Tél : 04 91 32 43 25
    Audrey GROSSI
    Tél : 04 91 32 45 80Unité

    mixte de formation continue en santé (UMFCS)
    Bureau des DU
    Faculté des sciences médicales et paramédicales

    Aix-Marseille

    Université
    27 bd Jean Moulin
    13385 Marseille cedex 05

  • Informations pratiques

    Training mode

    Presential

    Rates

    • Initial training:
    • €534Continuing
    • training
    • : €1,369